Most are designed to target rare genetic diseases, including haemophilia B, where mutation causes problems with blood clotting.

大多数药物旨在针对罕见的遗传疾病，包括 B 型血友病，这种疾病的突变会导致凝血问题。

So far, the new generation of genomic medicines have been eye-wateringly expensive—a shot of Hemgenix, a haemophilia B gene-therapy, costs $3.5m, around a million dollars more than Casgevy.

到目前为止，新一代基因药物的价格令人瞠目结舌，一剂血友病 B 基因治疗药物 Hemgenix 就要花费 350 万美元，比 Casgevy 贵出约 100 万美元。